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Category
Medicines
Hemostatic agent
Nitrogen-binding agents
Haematology
RNAi Therapeutics
Thrombolytic agents
Duchenne muscular dystrophy
Arthritis
Oncology
Lysosomal enzymes
Immunosuppressant
Macular degeneration agents
Enzyme-replacement therapy
Hormones
IDH1 and IDH2 inhibitors
Monoclonal antibodies
Spinal mus. atrophy
CFTR modulators
Ophthalmology
Anti-viral
Kinase inhibitors
Transthyretin (TTR) stabilizer
Hematopoietic agent
Hepatology
C-type natriuretic peptide (CNP) analog
Cardiovascular
Myasthenia gravis
Antisense oligonucleotides
Dermatology
Immunomodulators
Hyperammonemia
Antibiotics
Janus kinase inhibitors
Sclerostin inhibitors
Recombinant antihemophilic factor
Respiratory
Thrombopoietin receptor agonist
RANK Ligand Inhibitor
Herbs
Laxative
Gynaecology
Supplements
L-carnitine
Vitamins
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Enzyme-replacement therapy
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NEXVIAZYME® for Injection
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