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Category
Medicines
Hemostatic agent
Bleeding disorder
Neuromuscular blocking agent
Haematology
RNAi Therapeutics
Thrombolytic agents
Arthritis
Oncology
Lysosomal enzymes
Immunosuppressant
Lipid-lowering agent
Enzyme-replacement therapy
Hormones
Monoclonal antibodies
Spinal mus. atrophy
CFTR modulators
Ophthalmology
Anabolic agent
Anti-viral
Transthyretin (TTR) stabilizer
Hematopoietic agent
Hepatology
Cardiovascular
Antimigraine agent
Myasthenia gravis
Dermatology
Immunomodulators
Hyperammonemia
Anti-fungal
Janus kinase inhibitors
Sclerostin inhibitors
Recombinant antihemophilic factor
Respiratory
RANK Ligand Inhibitor
Herbs
Laxative
Gynaecology
Supplements
L-carnitine
Vitamins
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Category "Tripeptidyl peptidase 1 (TPP1) deficiency"
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Lysosomal enzymes
Medicines
BRINEURA® Injection 150mg
$
27,000.00
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